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Functional correction of CNS lesions in an MPS-IIIA mouse model by intracerebral AAV-mediated delivery of sulfamidase and SUMF1 genes

scientific article published on 27 August 2007

Author/s

author: Kim Hemsley, Adeline A. Lau, Alessia Lombardi, Alberto Auricchio, Andrea Ballabio, John Hopwood

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Work details

Publication date
August 27, 2007
- -
Language
English

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