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Selection-free gene repair after adenoviral vector transduction of designer nucleases: rescue of dystrophin synthesis in DMD muscle cell populations.

scientific article published on 13 January 2016

Author/s

author: Vincent Mouly, Luca Stefanucci, Josephine M Janssen, Xiaoyu Chen, Manuel A F V Gonçalves, Ignazio Maggio

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Work details

Publication date
January 13, 2016
- -
Language
English

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