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Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration

scientific article

Author/s

author: Sandro Banfi, Jennifer Wellman McDonnell, Enrico M. Surace, Francesco Testa, Francesca Simonelli, Eric A Pierce, Sandro Banfi, Alberto Auricchio, Settimio Rossi, Albert M Maguire, Kathleen Marshall, Federico Mingozzi

Wikidata


Work details

Publication date
December 1, 2009
- -
Language
English

Copyright status